FDA rare diseases list

Landscape-Ad-No-URLThe 8-week reprieve from sequestration has benefited all federal discretionary programs. “Live to fight another day” is not to be taken for granted. Sequestration still, however, looms as an existential threat to the mission of the FDA. If it occurs …

Inside Health

FDA’s preliminary list of 20 disease areas it may focus on as part of the patient-focused drug development initiative mandated by the FDA Safety and Innovation Act has led to in-fighting among patient advocacy …

Rep. Erik Paulsen tells MassDevice.com that congress wants higher user fees to come with greater accountability.

Some members of congress are calling for the FDA to provide quarterly reports on the agency’s progress …

One Hundred Twelfth Congress of the United States of America

An Act To amend the Federal Food, Drug, and Cosmetic Act to revise and extend the user-fee programs for prescription drugs and medical devices, to establish user-fee programs for generic drugs and …

Obesity treatments, life-saving antibiotics and other drugs deemed to offer societal benefit despite their risks may get speedier U.S. approvals under plans being discussed to better balance innovation and safety.…

As part of the performance commitments of the fifth authorization of the Prescription Drug User Fee Act (PDUFA V), FDA has published a notice in the Federal Register related to Patient-Focused Drug Development, an initiative that provides for a more …

Complete the survey and be entered to win a $50 gift card!

ACT UP and their colleagues fought for nine years before winning life-saving medications. They organized a mass movement, they took to the streets, they made art, they made noise, they made a difference. Their tools included clear demands, arresting graphics, …

The POLITICO Pro Health care team takes an in-depth look at the future and policies of the FDA. Special guests include: Friends of Cancer Research’s Dr. Jeff Allen; The Pew Charitable Health Group’s Allan Coukell; Biotechnology Industry Organization’s …

Popular Q&A

avatar
Can you NAme a list of rare diseases please?

List of rare diseases: 5-Oxoprolinuria, Aarskog Syndrome, Aase Syndrome, Abetalipoproteinemia, & Ablepharon Macrostomia Syndrome

Related Posts